Stem Cell & Gene Therapy for Fatal Bubble Baby Disease (SCID)
This video tells the story of a brave young patient, Ronnie, and his parents who decided to participate in a CIRM-funded trial run by UC San Francisco and St. Jude Children’s Research Hospital in an attempt to save Ronnie’s life from an often-fatal disease called severe combined immunodeficiency (SCID). This disorder, also known as bubble baby disease, leaves newborns without a functioning immune system which can turn a simple cold into a potentially deadly infection.