Disease Focus: Blood Disorders


Defeating Sickle Cell Disease with Stem Cells + Gene Therapy

Using a mix of science, humor and easy to understand language, this video describes sickle cell disease and a CIRM-funded clinical trial at UCLA that is testing a stem cell and gene therapy cure. This awful genetic disorder causes red blood cells to assume a sickle shape, clogging blood vessels and producing episodes of excruciating […]

Spotlight on Amyloidosis and Stem Cell Research: Robert Vescio MD – Cedars-Sinai

Dr. Robert Vescio spoke to CIRM’s governing board to promote awareness about amyloidosis, a rare, often fatal disease caused by the abnormal deposit of proteins called amyloids in various tissues of the body. Dr. Vescio, director of Cedars-Sinai’s multiple myeloma and amyloidosis program, explained the disease and described the current stem cell based treatment options. […]

Michael York: Amyloidosis and Stem Cell Research

Michael York, star of films such as Cabaret, Logan’s Run, and Austin Powers, spoke to the California stem cell agency governing board about his personal battle with amyloidosis, a rare, often fatal disease caused by the abnormal deposit of proteins called amyloids in various tissues of the body. In addition to amyloidosis, York was also […]

William Kim, UCLA – CIRM Stem Cell #SciencePitch

Catriona Jamieson, UCSD – CIRM Stem Cell #SciencePitch

Spotlight on Genomics: Understanding Our Genes

This seminar, presented to the CIRM governing board on January 17th, 2012, provides a glimpse into a future of personalized medicine in which genomics, the study of genes and their function, is applied to pinpoint specific treatments for patients. Speakers included Craig Venter, president and founder of the J. Craig Venter Institute, Catriona Jamieson, director […]

Catriona Jamieson – UCSD | CIRM Spotlight on Genomics

This seminar, presented to the California Institute for Regenerative Medicine governing board on January 17th, 2012, provides a glimpse into a future of personalized medicine in which genomics, the study of genes and their function, is applied to pinpoint specific treatments for patients. Speakers include Catriona Jamieson, director for stem cell research at the UCSD […]

Spotlight on Genomics: Clinical Trial for Myelofibrosis that Targets Cancer Stem Cells

Four minute excerpt from the Spotlight on Genomics seminar presentation at the January 17th 2012 CIRM governing board meeting. The video features a conversation between Catriona Jamieson, director for stem cell research at UCSD Moores Cancer Center, and one of her patients who is participating in a clinical trial for the treatment of myelofibrosis, a […]

Stem Cell Gene Therapy for Sickle Cell Anemia – Donald Kohn

CIRM has funded a $9 million disease team to develop a more effective and safer bone marrow transplant to treat sickle cell disease. The team is led by Dr. Donald Kohn, director of the Human Gene Medicine Program at UCLA, a scientist with the Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell […]

Spotlight on Basic Research: Irv Weissman

Irv Weissman, Ph.D., spoke at the “Spotlight on Basic Research,” an educational event presented at the CIRM Governing Board meeting on August 20, 2009. Weissman has a CIRM Comprehensive grant to identify cell surface markers on human embryonic stem cells that distinguish differentiated cells from potentially tumorigenic cells. He also has a CIRM Disease Team […]