Efficacy and safety of cryopreserved autologous CD34+ HSC transduced with EFS-ADA lentiviral vector encoding for human ADA gene in ADA-SCID subjects

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Grant Award Details

Grant Number:
CLIN2-17078
Investigator(s):
Human Stem Cell Use:
Award Value:
$14,325,181
Status:
Active

Grant Application Details

Application Title:

Efficacy and safety of cryopreserved autologous CD34+ HSC transduced with EFS-ADA lentiviral vector encoding for human ADA gene in ADA-SCID subjects