Evaluation of an ex vivo lentiviral gene therapy for the treatment of Angelman syndrome

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Grant Award Details

Grant Number:
TRAN1-16965
Investigator(s):
Human Stem Cell Use:
Award Value:
$5,276,765
Status:
Pre-Active

Grant Application Details

Application Title:

Evaluation of an ex vivo lentiviral gene therapy for the treatment of Angelman syndrome