Therapeutic Translational Research Projects | University of California, Los Angeles | Development of a Gene Therapy for Treatment of Guanidinoacetate Methyltransferase Deficiency-Translating In Vivo Proof of Concept to Support a Pre-IND |
$5,145,825 |
Therapeutic Translational Research Projects | University of California, Los Angeles | Development of a Gene Therapy for the Treatment of Arginase Deficiency – Translating from Proof of Concept to Support Pre-IND Meeting |
$5,266,504 |