| Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1. |
2019 |
N Engl J Med |
| Lentiviral Gene Therapy with Low Dose Busulfan for Infants with X-Linked Severe Combined Immune Deficiency (XSCID) results in the Development of a Normal and Sustained Immune System: Interim Results of an ongoing Phase I/II Clinical Study |
2019 |
ASGCT |
| LIM homeobox 2 promotes interaction between human iPS-derived hepatic progenitors and iPS-derived hepatic stellate-like cells. |
2019 |
Sci Rep |
| Long-term ex vivo haematopoietic-stem-cell expansion allows nonconditioned transplantation. |
2019 |
Nature |
| LRRK2 modifies alpha-syn pathology and spread in mouse models and human neurons. |
2019 |
Acta Neuropathol |
| Macrophage polarization impacts tunneling nanotube formation and intercellular organelle trafficking. |
2019 |
Sci Rep |
| Mesenchymal Stem Cells Reduce Corneal Fibrosis and Inflammation via Extracellular Vesicle-Mediated Delivery of miRNA. |
2019 |
Stem Cells Transl Med |
| Mesenchymal Stromal Cells Are Required for Regeneration and Homeostatic Maintenance of Skeletal Muscle. |
2019 |
Cell Rep |
| Metabolic and Organelle Morphology Defects in Mice and Human Patients Define Spinocerebellar Ataxia Type 7 as a Mitochondrial Disease. |
2019 |
Cell Rep |
| Methotrexate Chemotherapy Induces Persistent Tri-glial Dysregulation that Underlies Chemotherapy-Related Cognitive Impairment. |
2019 |
Cell |
| Mitigating Antagonism between Transcription and Proliferation Allows Near-Deterministic Cellular Reprogramming. |
2019 |
Cell Stem Cell |
| Modeling Snyder-Robinson Syndrome in multipotent stromal cells reveals impaired mitochondrial function as a potential cause for deficient osteogenesis. |
2019 |
Sci Rep |
| Modeling Spatial Correlation of Transcripts with Application to Developing Pancreas. |
2019 |
Sci Rep |
| Multiscale, multispectral fluorescence lifetime imaging using a double-clad fiber. |
2019 |
Opt Lett |
| Neuroprotective effect of placenta-derived mesenchymal stromal cells: role of exosomes. |
2019 |
FASEB J |
| Notch Inhibition Prevents Differentiation of Human Limbal Stem/Progenitor Cells in vitro. |
2019 |
Sci Rep |
| Off-the-shelf cell therapy with induced pluripotent stem cell-derived natural killer cells. |
2019 |
Semin Immunopathol |
| Online measurement of oxygen enables continuous noninvasive evaluation of human-induced pluripotent stem cell (hiPSC) culture in a perfused 3D hollow-fiber bioreactor. |
2019 |
J Tissue Eng Regen Med |
| Paramagnetic Fluorinated Nanoemulsions for in vivo F-19 MRI. |
2019 |
Mol Imaging Biol |
| Phenotypic Variation Between Stromal Cells Differentially Impacts Engineered Cardiac Tissue Function. |
2019 |
Tissue Eng Part A |
| Potential long-term treatment of hemophilia A by neonatal co-transplantation of cord blood-derived endothelial colony-forming cells and placental mesenchymal stromal cells. |
2019 |
Stem Cell Res Ther |
| Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction. |
2019 |
Cell Res |
| Preliminary Results of a Phase 1/2 Clinical Study of Zinc Finger Nuclease-Mediated Editing of BCL11A in Autologous Hematopoietic Stem Cells for Transfusion-Dependent Beta Thalassemia |
2019 |
Blood |
| Primed mesenchymal stem cells package exosomes with metabolites associated with immunomodulation. |
2019 |
Biochem Biophys Res Commun |
| Promoting remyelination through cell transplantation therapies in a model of viral-induced neurodegenerative disease. |
2019 |
Dev Dyn |
| Proteomic analyses reveal misregulation of LIN28 expression and delayed timing of glial differentiation in human iPS cells with MECP2 loss-of-function. |
2019 |
PLoS One |
| PTPsigma inhibitors promote hematopoietic stem cell regeneration. |
2019 |
Nat Commun |
| Receptor subtype discrimination using extensive shape complementary designed interfaces. |
2019 |
Nat Struct Mol Biol |
| Selective hematopoietic stem cell ablation using CD117-antibody-drug-conjugates enables safe and effective transplantation with immunity preservation. |
2019 |
Nat Commun |
| Single cell analysis of human foetal liver captures the transcriptional profile of hepatobiliary hybrid progenitors. |
2019 |
Nat Commun |
| Single-cell genomics identifies cell type-specific molecular changes in autism. |
2019 |
Science |
| Skeletal Stem Cell-Schwann Cell Circuitry in Mandibular Repair. |
2019 |
Cell Rep |
| Species-specific maturation profiles of human, chimpanzee and bonobo neural cells. |
2019 |
Elife |
| Spinal Angulation: A Limitation of the Fetal Lamb Model of Myelomeningocele. |
2019 |
Fetal Diagn Ther |
| Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS. |
2019 |
Nat Med |
| Sufficiency for inducible Caspase-9 safety switch in human pluripotent stem cells and disease cells. |
2019 |
Gene Ther |
| Systematic genetic analysis of the MHC region reveals mechanistic underpinnings of HLA type associations with disease. |
2019 |
Elife |
| T cell antigen discovery via signaling and antigen-presenting bifunctional receptors. |
2019 |
Nat Methods |
| TFAP2C- and p63-Dependent Networks Sequentially Rearrange Chromatin Landscapes to Drive Human Epidermal Lineage Commitment. |
2019 |
Cell Stem Cell |
| The application of human amniotic membrane in the surgical management of limbal stem cell deficiency. |
2019 |
Ocul Surf |
| The lymphoid-associated interleukin 7 receptor (IL7R) regulates tissue-resident macrophage development. |
2019 |
Development |
| The role of cellular interactions in the induction of hepatocyte polarity and functional maturation in stem cell-derived hepatic cells. |
2019 |
Differentiation |
| Transposable Elements, Inflammation, and Neurological Disease. |
2019 |
Front Neurol |
| Use of polyvinyl alcohol for chimeric antigen receptor T-cell expansion. |
2019 |
Exp Hematol |
| Using the Inducible Caspase-9 Suicide-Safeguard System with iPSC and Bioluminescent Tracking. |
2019 |
Methods Mol Biol |
| V2a interneuron differentiation from mouse and human pluripotent stem cells. |
2019 |
Nat Protoc |
| Video-based kinetic analysis of calcification in live osteogenic human embryonic stem cell cultures reveals the developmentally toxic effect of Snus tobacco extract. |
2019 |
Toxicol Appl Pharmacol |
| Wnt signaling inhibition by monensin results in a period of Hippo pathway activation during intestinal adaptation in zebrafish. |
2019 |
Am J Physiol Gastrointest Liver Physiol |
| Wnt Signaling Is Required for the Maintenance of Human Limbal Stem/Progenitor Cells In Vitro. |
2019 |
Invest Ophthalmol Vis Sci |
| A bioengineered retinal pigment epithelial monolayer for advanced, dry age-related macular degeneration. |
2018 |
Sci Transl Med |
